Understanding Neuromuscular disease

Giving to Newcastle: the TREAT-NMD Alliance

Rare neuromuscular disorders can be hugely debilitating and chronic conditions and at present there are no treatments or therapies to prevent or cure their symptoms.

Newcastle leads a global research network called the TREAT-NMD Alliance which provides the infrastructure to enable research experts across the world to collaborate and work towards better diagnosis and treatment. Together the Alliance aims to reduce the bottlenecks currently delaying the progression of treatments through development of patient registries, validation of outcome measures and improvement in standards of care.

By supporting the work of the TREAT-NMD Alliance secretariat in Newcastle you can support the work of the network across the globe in helping to improve the lives of those living with inherited neuromuscular disorders.

"By acting as catalyst in developing standards of care, advancing clinical research, providing expertise in outcome measure development and leading the creation of national patient registries, TREAT-NMD is a key partner in the development of ataluren and a guide to PTC as we advance our efforts in Duchenne Muscular Dystrophy." (PTC Therapeutics)

For more information: www.ncl.ac.uk/igm/services/muscle

www.treat-nmd.eu/about/network/donate 

There are many ways that you can donate to the TREAT-NMD Alliance. Please open the how to donate page to find out more.

Prof. Annemieke Aartsma-Rus
A visiting Professor at the Institute of Genetic Medicine from Leiden University Medical Centre has been instrumental in developing exon skipping therapies for Duchene muscular dystrophy.
Professor Hanns Lochmüller
A Professor of Experimental Myology at the Institute of Genetic Medicine, Professor Lochmüller heads the muscle team at Newcastle with Professors Kate Bushby and Volker Straub.