Promoter dependence of plasmid-pluronics targeted alpha galactosidase A expression in skeletal muscle of Fabry mice (2005)

Author(s): Lavigne MD, Pohlschmidt M, Novo JF, Higgins B, Alakhov V, Lochmuller H, Sakuraba H, Goldspink G, MacDermot K, Gorecki DC

      • Date: 01-11-2005
      • Journal: Molecular Therapy
      • Volume: 12
      • Issue: 5
      • Pages: 985-990
      • Publisher: Nature Publishing Group
      • Publication type: Article
      • Bibliographic status: Published

      Keywords: Animals Antibodies/blood CD8-Positive T-Lymphocytes Fabry Disease/genetics/immunology/ metabolism/therapy Gene Therapy Genetic Vectors Mice Muscle, Skeletal/ metabolism Plasmids/genetics Promoter Regions (Genetics) alpha-Galactosidase/ genetics/immunology/metabolism


      Professor Hanns Lochmuller
      Professor of Experimental Myology