Author(s): Lavigne MD, Pohlschmidt M, Novo JF, Higgins B, Alakhov V, Lochmuller H, Sakuraba H, Goldspink G, MacDermot K, Gorecki DC
Keywords: Animals Antibodies/blood CD8-Positive T-Lymphocytes Fabry Disease/genetics/immunology/ metabolism/therapy Gene Therapy Genetic Vectors Mice Muscle, Skeletal/ metabolism Plasmids/genetics Promoter Regions (Genetics) alpha-Galactosidase/ genetics/immunology/metabolism
|
Professor Hanns Lochmuller
|
|